Proprietary lipid nanoparticle for in vivo kidney delivery.
Stargardt Disease
Undisclosed
Autosomal Dominant Polycystic Kidney Disease
(due to mutations in PKD1 gene)
Autosomal Dominant Polycystic Kidney Disease
(due to mutations in PKD2 gene)
Autosomal Recessive Polycystic Kidney Disease
Tubulointerstitial Kidney Disease
